View Full Version : Gene therapy works in cystic fibrosis for the first time

Jean M
07-04-2015, 07:40 PM

Twenty six years after the gene responsible for cystic fibrosis was identified, researchers have shown that people with the lung-damaging condition can benefit from gene therapy. The improvement on lung function is small just 3.7 per cent compared with a placebo group but it validates the decades that researchers have spent trying to find a way to put healthy copies of the faulty gene into the lung cells of people with cystic fibrosis.